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Structure-guided design of endosomolytic chloroquine-like lipid nanoparticles for mRNA delivery and genome editing

Nature Communications. 2025-05; 
Zhen Liu, Jiacai Wu, Ning Wang, Yongqi Lin, Ruiteng Song, Min Zhang, Bin Li
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Custom RNAi Services Ai9 mice were intramuscularly injected with ecoLNPs containing 1 mg kg−1 total RNA dose of Cas9 mRNA (APExBio) and gRNA (AAGTAAAACCTCTACAAATG, GenScript) targeting the loxP-flanked stop cassette locus at weight ratio of 3:1 on day 0 and day 7. Get A Quote

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